We want to hear from the Pompe community.
Recent reports of supply constraints affecting Pompe enzyme replacement therapies have raised concerns about delayed or interrupted infusions for some patients and families.
This survey is designed to better understand the experiences of individuals living with Pompe disease and their caregivers, including whether an upcoming Nexviazyme/Nexviadyme infusion has been delayed or interrupted, how patients and families were informed, how long any delay lasted, and what impact the situation has had on care and daily life.
Your responses will help patient advocates and the broader Pompe community better understand the scope and impact of these supply challenges, identify gaps in communication and support, and advocate for greater transparency and continuity of care.
The survey should take approximately 5–7 minutes to complete.